Jwheel86 Posted August 29, 2018 Share Posted August 29, 2018 Best article I could find: https://endpts.com/biogens-big-breakthrough-drug-spinraza-runs-into-a-barrier-as-nice-turns-thumbs-down-on-reimbursement/ The UK has decided not to cover Spinraza, the first drug to treat Spinal Muscular Atrophy (leading genetic cause of infant death), even in cases where the drug can prevent symptoms entirely. They argue there is no long term studies and no evidence it will save NHS money. I'm not surprised they aren't covering it in adults, there you can kind of make an argument, but not covering kids, including "dead before 2" Type 1 kids is mind blowing cruel. Quote Link to comment Share on other sites More sharing options...
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